(Duke University) Researchers at Duke University have shown that a single systemic treatment using CRISPR genome editing technology can safely and stably correct a genetic disease -- Duchenne muscular dystrophy (DMD) -- for more than a year in mice, despite observed immune responses and alternative gene editing outcomes.
from EurekAlert! - Technology, Engineering and Computer Science http://bit.ly/2EfYlSq
Tuesday, February 19, 2019
Single CRISPR treatment provides long-term benefits in mice
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